Smirnikhina, Svetlana A.; Kondrateva, Ekaterina V.; Adilgereeva, Elmira P.; Anuchina, Arina A.; Zaynitdinova, Milyausha I.; Slesarenko, Yana S.; Ershova, Angelina S.; Ustinov, Kirill D.; Yasinovsky, Matvei I.; Amelina, Elena L.; Voronina, Ekaterina S.; Yakushina, Valentina D.; Tabakov, Vyacheslav Yu.; Lavrov, Alexander V.
(Public Library of Science, 2020-11-11)
Development of genome editing methods created new opportunities for the development of
etiology-based therapies of hereditary diseases. Here, we demonstrate that CRISPR/Cas9
can correct p.F508del mutation in the CFTR ...
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